Gene-Targeted Therapies in Pediatric Neurology: Challenges and Opportunities in Diagnosis and Delivery
Renée A. Shellhaas, Gabrielle deVeber, Joshua L. Bonkowsky, Erika F. Augustine, Alexander G. Bassuk, Daniel G. Calame, Melisa Carrasco, Nomazulu Dlamini, Ryan J. Felling, Hannah C. Glass, Zachary M. Grinspan, Réjean M. Guerriero, Angela Hewitt, Shafali Jeste, Juliet K. Knowles, Ariel M. Lyons‐Warren, Stephen M. Maricich, Patricia L. Musolino, G. Praveen Raju, Jong M. Rho, Alexander Rotenberg, Elliott H. Sherr, Janet S. Soul, Julie Ziobro
Topics & Concepts
MedicineNeurologyDiseaseClinical trialIntensive care medicinePathologyPsychiatryHereditary Neurological DisordersVirus-based gene therapy researchGenomics and Rare Diseases