IN VIVO CRISPR/CAS9 EDITING OF KLKB1 IN PATIENTS WITH HEREDITARY ANGIOEDEMA: A FIRST-IN-HUMAN STUDY

H. Longhurst, L. Fijen, K. Lindsay, J. Butler, A. Golden, D. Maag, Y. Xu, D. Cohn

2022Annals of Allergy Asthma & Immunology15 citationsDOI

Topics & Concepts

MedicineCRISPRHereditary angioedemaGenome editingIn vivoAngioedemaDermatologyGeneticsComputational biologyGeneBiologyCRISPR and Genetic EngineeringBiotechnology and Related Fields