Lomitapide for the treatment of paediatric patients with homozygous familial hypercholesterolaemia (APH-19): results from the efficacy phase of an open-label, multicentre, phase 3 study
L. Masana, Zambon Alberto, Claus Peter Schmitt, Christina Taylan, Joenna Driemeyer, Hofit Cohen, Paola Sabrina Buonuomo, Abdullah Al‐Ashwal, Mohammed Al-Dubayee, Naji Kholaif, José Luis Díaz-Díaz, Faouzi Maatouk, Sergio Martínez‐Hervás, Brian Mangal, Sandra Löwe, Tracy Cunningham
Topics & Concepts
MedicinePhase (matter)Open labelPediatricsInternal medicineIntensive care medicineClinical trialChemistryOrganic chemistryLipoproteins and Cardiovascular HealthDiabetes, Cardiovascular Risks, and LipoproteinsCholesterol and Lipid Metabolism