Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy
James M. Wilson, Terence R. Flotte
Topics & Concepts
Genetic enhancementMyopathyMedicineGenePhysical medicine and rehabilitationOncologyInternal medicineGeneticsBiologyNeurogenetic and Muscular Disorders ResearchHearing, Cochlea, Tinnitus, GeneticsCellular transport and secretion