Litcius/Paper detail

Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy

James M. Wilson, Terence R. Flotte

2020Human Gene Therapy200 citationsDOI

Topics & Concepts

Genetic enhancementMyopathyMedicineGenePhysical medicine and rehabilitationOncologyInternal medicineGeneticsBiologyNeurogenetic and Muscular Disorders ResearchHearing, Cochlea, Tinnitus, GeneticsCellular transport and secretion