Challenges and opportunities in spinal muscular atrophy therapeutics
Crystal Jing Jing Yeo, Eduardo F. Tizzano, Basil T. Darras
Topics & Concepts
Spinal muscular atrophyMedicineDiseaseAtrophyBioinformaticsPediatricsNeuromuscular diseaseQuality of life (healthcare)In uteroMotor neuronIntensive care medicinePathologyPregnancyFetusNursingGeneticsBiologyNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery