Litcius/Paper detail

α-Synuclein Locus Triplication Causes Parkinson's Disease

A. B. Singleton, Andrew Singleton, Matthew J. Farrer, Janel Johnson, Andrew Singleton, A. Singleton, Stephen Hague, Jennifer M. Kachergus, Mary Hulihan, Terhi Peuralinna, A. Dutra, Robert Nussbaum, S. Lincoln, Anthony Crawley, M Hanson, Demetrius M. Maraganore, Charles H. Adler, Mark Cookson, Manfred D. Muenter, Maria Fortuna Baptista, David W. Miller, Jan Blancato, John Hardy, Katrina Gwinn

2003Science4,415 citationsDOI

Abstract

Impaired Autophagic-Lysosomal Fusion in Parkinson's Patient Midbrain Neurons Occurs through Loss of ykt6 and Is Rescued by Farnesyltransferase Inhibition,

Topics & Concepts

Parkinson's diseaseLocus (genetics)DiseaseNeuroscienceGeneticsBiologyMedicineInternal medicineGeneParkinson's Disease Mechanisms and TreatmentsNeurological disorders and treatmentsNuclear Receptors and Signaling