Genetic correction strategies for Duchenne muscular dystrophy and their impact on the heart
Jamie R. Johnston, Elizabeth M. McNally
Topics & Concepts
DystrophinDuchenne muscular dystrophyMedicineMuscular dystrophyCardiomyopathyExon skippingSkeletal muscleBioinformaticsmdx mouseGeneticsExonGeneHeart failureCardiologyInternal medicineBiologyAlternative splicingMuscle Physiology and DisordersCardiomyopathy and Myosin StudiesCRISPR and Genetic Engineering