Evaluating the efficacy and safety of pozelimab in patients with CD55 deficiency with hyperactivation of complement, angiopathic thrombosis, and protein-losing enteropathy disease: an open-label phase 2 and 3 study
Ahmet Özen, Voranush Chongsrisawat, Asena Pınar Sefer, Burcu Kolukısa, Jessica J. Jalbert, Karoline A. Meagher, Taylor Brackin, Hagit Baris Feldman, Safa Barış, Elif Karakoç-Aydıner, Rabia Ergelen, Ivan J. Fuss, Heather Moorman, Narissara Suratannon, Kanya Suphapeetiporn, Lorah Perlee, Olivier Harari, George D. Yancopoulos, Michael J. Lenardo, Jutta Miller, Orly Eshach Adiv, Sevgi Bilgiç Eltan, Melek Yorgun Altunbaş, Mary Magliocco, Helen Matthews, Beatriz E. Marciano, Pantipa Chatchatee, Caryn F. Trbovic, Michael E. Burczynski, Umesh Chaudhari, Yusuf Usta, Cansu Altuntaş, Sibel Yavuz, Ahmet Baştürk, Fatma Demirbaş, Erdem Topal, Ayhan Gazi Kalaycı, Wanlapa Weerapakorn, A MARTINEZ, Adriana Bottero
Topics & Concepts
MedicineEnteropathyInternal medicineGastroenterologyThrombosisSurgeryDiseaseComplement system in diseasesLymphatic Disorders and TreatmentsRenal Diseases and Glomerulopathies