Challenges in Gaucher disease: Perspectives from an expert panel
Gregory A. Grabowski, Priya S. Kishnani, Roy N. Alcalay, S. Grace Prakalapakorn, Barry E. Rosenbloom, Dominick A Tuason, Neal J. Weinreb
Topics & Concepts
DiseaseGlucocerebrosidaseMedicinePathologyLysosomal Storage Disorders ResearchStudies on Chitinases and ChitosanasesCellular transport and secretion