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Safety and efficacy of propranolol for treatment of familial cerebral cavernous malformations (Treat_CCM): a randomised, open-label, blinded-endpoint, phase 2 pilot trial

Silvia Lanfranconi, Elisa Scola, Jennifer Meessen, Roberto Pallini, Giulio Bertani, Rustam Al‐Shahi Salman, Elisabetta Dejana, Roberto Latini, Giorgia Abete Fornara, Nicolò M. Agnelli, Alessio Albanese, Issam A. Awad, Renzo Bagnati, Giovanna Balconi, Elena Ballabio, Ettore Beghi, Roberto Bernasconi, Giulio Bertani, Silvia Besana, Adriana Blanda, Chiara Bossi, Nereo Bresolin, Maria G. Buratti, Roberta Calabrese, Maria Rita Carriero, Marco Castori, Elisa F. Ciceri, Rossella Ciurleo, Giacomo P. Comi, Valeria Elisa Contarino, Giorgio Conte, Leonardo D’Agruma, Giorgio Q. D'Alessandris, Ugo de Grazia, Rina Di Bonaventura, Piergiorgio d’Orio, Giuseppe Faragò, Andreana Foresta, Carmela Fusco, Chiara Gaudino, Maria Grazia Lampugnani, Alessia Lanno, Francesca Lazzaroni, Cornelia Lee, Marco Locatelli, Aldo P. Maggioni, Peetra U. Magnusson, Matteo Malinverno, Maurizio Mangiavacchi, Antonella Mangraviti, Silvia Marino, Selene Mazzola, Enrico Nicolis, Deborah Novelli, Maria L. Ojeda Fernandez, Antonio Petracca, Fabrizio Pignotti, Simona Pogliani, M. Poloni, A. Prelle, Pamela Raggi, Franca Raucci, Caroline Regna‐Gladin, Dario Ronchi, Emma Scelzo, Salim Abdelilah‐Seyfried, Anna Simeone, Carmelo Lucio Sturiale, Laura Tassi, Mauro Tettamanti, Valter Torri, Elisabeth Tournier‐Lasserve, Rita Treglia, Fabio Triulzi, Celeste Ungaro, Elison Ursi, Gloria Valcamonica, Antonella Vasamì, Barbara Zarino

2022The Lancet Neurology62 citationsDOIOpen Access PDF

Topics & Concepts

MedicineClinical endpointClinical trialRandomized controlled trialPediatricsPopulationIntention-to-treat analysisIncidence (geometry)Physical therapySurgeryInternal medicineOpticsPhysicsEnvironmental healthVascular Malformations Diagnosis and TreatmentVascular Malformations and HemangiomasIntracerebral and Subarachnoid Hemorrhage Research
Safety and efficacy of propranolol for treatment of familial cerebral cavernous malformations (Treat_CCM): a randomised, open-label, blinded-endpoint, phase 2 pilot trial | Litcius