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Defining Efficacy Estimands in Clinical Trials: Examples Illustrating ICH E9(R1) Guidelines

Bohdana Ratitch, Niti Goel, Craig Mallinckrodt, James Bell, Jonathan W. Bartlett, Geert Molenberghs, Pritibha Singh, Ilya Lipkovich, Michael O’Kelly

2020Therapeutic Innovation & Regulatory Science39 citationsDOIOpen Access PDF

Topics & Concepts

PharmacyManagement scienceClinical trialComputer sciencePsychologyOutcomes researchProcess (computing)MedicineAlternative medicineFamily medicineEconomicsOperating systemPathologyStatistical Methods in Clinical TrialsHealth Systems, Economic Evaluations, Quality of LifeAdvanced Causal Inference Techniques
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