Adenosine Deaminase (ADA)–Deficient Severe Combined Immune Deficiency (SCID) in the US Immunodeficiency Network (USIDNet) Registry
Caroline Y. Kuo, Elizabeth Garabedian, Jennifer M. Puck, Morton J. Cowan, Kathleen E. Sullivan, Rebecca H. Buckley, Charlotte Cunningham‐Rundles, Rebecca Marsh, Fabio Candotti, Donald B. Kohn
Topics & Concepts
MedicineSevere combined immunodeficiencyAdenosine deaminase deficiencyPediatricsHematopoietic stem cell transplantationAdenosine deaminaseImmunodeficiencyCord bloodInternal medicinePrimary immunodeficiencyNewborn screeningBone marrowImmunologyImmune systemTransplantationBiologyAdenosineGeneBiochemistryImmunodeficiency and Autoimmune DisordersParvovirus B19 Infection StudiesVirus-based gene therapy research