Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in adults with non-transfusion dependent α-thalassaemia or β-thalassaemia: an open-label, multicentre, phase 2 study

Kevin H.M. Kuo, D. Mark Layton, Ashutosh Lal, Hanny Al‐Samkari, Joy Bhatia, Penelope A. Kosinski, Tong Bo, Megan Suzanne Lynch, Katrin Uhlig, Elliott Vichinsky